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Standardized Data Structures in Rare Diseases: CDISC User Guides for Duchenne Muscular Dystrophy and Huntington’s Disease

Mullin, Ariana P; Corey, Diane; Turner, Emily C; Liwski, Richard; Olson, Daniel; et al.  Clinical and Translational Science Vol. 14, Iss. 1,  (Jan 2021): 214-221.

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