Title
New disease modifying therapies for two genetic childhood-onset neurometabolic disorders (metachromatic leucodystrophy and adrenoleucodystrophy)
Author
Federico, Antonio 1 ; de Visser Marianne 2
1 University of Siena, Department of Medicine, Surgery and Neurosciences, Medical School, Siena, Italy (GRID:grid.9024.f) (ISNI:0000 0004 1757 4641)
2 Amsterdam University Medical Centres, Department of Neurology, Amsterdam, The Netherlands (GRID:grid.509540.d) (ISNI:0000 0004 6880 3010)
Publication date
Jul 2021
Source type
Scholarly Journal
Language of publication
English
ProQuest document ID
2549111099
Copyright
© Fondazione Società Italiana di Neurologia 2021.