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Title
New disease modifying therapies for two genetic childhood-onset neurometabolic disorders (metachromatic leucodystrophy and adrenoleucodystrophy)
Author
Federico, Antonio 1 ; de Visser Marianne 2 

 University of Siena, Department of Medicine, Surgery and Neurosciences, Medical School, Siena, Italy (GRID:grid.9024.f) (ISNI:0000 0004 1757 4641) 
 Amsterdam University Medical Centres, Department of Neurology, Amsterdam, The Netherlands (GRID:grid.509540.d) (ISNI:0000 0004 6880 3010) 
Pages
2603-2606
Publication year
2021
Publication date
Jul 2021
Publisher
Springer Nature B.V.
ISSN
15901874
e-ISSN
15903478
Source type
Scholarly Journal
Language of publication
English
ProQuest document ID
2549111099
Copyright
© Fondazione Società Italiana di Neurologia 2021.