Abstract

Paroxysmal nocturnal hemoglobinuria (PNH) results from a mutation in the phosphatidylinositol glycan class-A gene which causes uncontrolled complement activation with resultant intravascular hemolysis and its sequelae. Eculizumab is a terminal complement inhibitor that blocks this complement activation and has revolutionized the treatment of PNH but comes with an enormous price which can have catastrophic health expenditure in low-middle income countries (LMIC) like Nepal. Here, we discuss the potential way forwards in the treatment of PNH in Nepal and other LMICs.

Details

Title
Eculizumab for paroxysmal nocturnal haemoglobinuria: catastrophic health expenditure in Nepalese patients
Author
Adhikari, Sugat; Sapkota, Surendra; Shrestha, Suraj; Karki, Kshitiz; Shrestha, Anjan
Pages
1-4
Section
Letter to the Editor
Publication year
2023
Publication date
2023
Publisher
BioMed Central
e-ISSN
17501172
Source type
Scholarly Journal
Language of publication
English
ProQuest document ID
2838788266
Copyright
© 2023. This work is licensed under http://creativecommons.org/licenses/by/4.0/ (the “License”). Notwithstanding the ProQuest Terms and Conditions, you may use this content in accordance with the terms of the License.