Abstract

Much progress has been made in understanding the pathophysiology and treatment of atypical hemolytic uremic syndrome (aHUS). Plasma therapy is the mainstay of treatment for aHUS. The availability of the first effective anti-complement therapeutic agent, eculizumab, has dramatically changed the outlook of this disease. However, its use in clinical practice raises important questions, such as who should receive the drug, when to start such therapy, and is it safe to stop treatment once the disease is controlled. We describe here for the 1 st time in India, use of eculizumab in a 12-year-old boy with aHUS. We also describe in this report challenges faced in procuring the drug, and an ideal, evidence-based method of treating aHUS in children.

Details

Title
Eculizumab for atypical hemolytic-uremic syndrome in India: First report from India and the challenges faced
Author
Sethi, S; Rohatgi, S; Dragon-Durey, M; Raghunathan, V; Dhaliwal, M; Rawat, A; Jha, P; Bansal, S; Raina, R; Kher, V
Publication year
2017
Publication date
Jan-Feb 2017
Publisher
Scientific Scholar
ISSN
09714065
e-ISSN
19983662
Source type
Scholarly Journal
Language of publication
English
ProQuest document ID
1856607830
Copyright
Copyright Medknow Publications & Media Pvt Ltd Jan-Feb 2017