Abstract

Congenital nephrogenic diabetes insipidus (NDI) is characterized by the inability of the kidney to concentrate urine. Congenital NDI is mainly caused by loss-of-function mutations in the vasopressin type 2 receptor (V2R), leading to impaired aquaporin-2 (AQP2) water channel activity. So far, treatment options of congenital NDI either by rescuing mutant V2R with chemical chaperones or by elevating cyclic adenosine monophosphate (cAMP) levels have failed to yield effective therapies. Here we show that inhibition of A-kinase anchoring proteins (AKAPs) binding to PKA increases PKA activity and activates AQP2 channels in cortical collecting duct cells. In vivo, the low molecular weight compound 3,3′-diamino-4,4′-dihydroxydiphenylmethane (FMP-API-1) and its derivatives increase AQP2 activity to the same extent as vasopressin, and increase urine osmolality in the context of V2R inhibition. We therefore suggest that FMP-API-1 may constitute a promising lead compound for the treatment of congenital NDI caused by V2R mutations.

Details

Title
AKAPs-PKA disruptors increase AQP2 activity independently of vasopressin in a model of nephrogenic diabetes insipidus
Author
Ando, Fumiaki 1 ; Mori, Shuichi 2 ; Yui, Naofumi 1 ; Morimoto, Tetsuji 3 ; Nomura, Naohiro 1 ; Sohara, Eisei 1 ; Rai, Tatemitsu 1 ; Sasaki, Sei 1 ; Kondo, Yoshiaki 4 ; Kagechika, Hiroyuki 2 ; Uchida, Shinichi 1 

 Department of Nephrology, Tokyo Medical and Dental University (TMDU), Tokyo, Japan 
 Institute of Biomaterials and Bioengineering, Tokyo Medical and Dental University (TMDU), Tokyo, Japan 
 Division of Pediatrics, Tohoku Medical and Pharmaceutical University, Miyagi, Japan 
 Department of Health Care Services Management, Nihon University School of Medicine, Tokyo, Japan 
Pages
1-11
Publication year
2018
Publication date
Apr 2018
Publisher
Nature Publishing Group
e-ISSN
20411723
Source type
Scholarly Journal
Language of publication
English
ProQuest document ID
2024454052
Copyright
© 2018. This work is published under http://creativecommons.org/licenses/by/4.0/ (the “License”). Notwithstanding the ProQuest Terms and Conditions, you may use this content in accordance with the terms of the License.